What is the Clinical Relevance of Splicing Enhancers?
The clinical relevance of splicing enhancers is significant, as they are potential targets for therapeutic interventions. Understanding the mechanisms by which splicing enhancers regulate gene expression can lead to the development of novel treatments for diseases caused by splicing defects. For instance, antisense oligonucleotides (ASOs) can be designed to modulate splicing by targeting specific enhancer sequences, offering a promising approach for treating genetic diseases.
