1. Identifying the Target Gene: Scientists first identify the specific gene or genes responsible for the disease. 2. Developing the Vector: A suitable vector (usually a virus) is developed to deliver the therapeutic gene into the patient's cells. 3. Delivery to Cells: The vector carrying the therapeutic gene is introduced into the patient's body, where it targets the affected cells. 4. Expression of the Gene: Once inside the cells, the therapeutic gene is expressed, producing the necessary proteins to correct the genetic defect or halt disease progression.
